From One Child to Many

GG’s story represents more than a single diagnosis—it represents a model for how rare disease, when met with coordination, rigor, and urgency, can catalyze scientific progress.

Support enables:

  • Functional and rescue studies in validated NAA15 cellular models

  • Advancement of gene-targeted and ASO-based strategies

  • Cross-disciplinary collaboration between clinicians and scientists

  • Data generation to inform compassionate-use and future trials

This work has implications not only for GG, but for other children affected by NAA15 haploinsufficiency and related neurogenetic conditions.

Let’s advance precision therapy together

3% Cover the Fee 
*Sweet Geej’s 501(c)(3) status is pending.
You can donate today or wait — either way, we’re grateful you’re here.